This journal focuses on the development, approval, and accessibility of orphan drugs for rare diseases. It covers therapeutic interventions for conditions such as rare cancers, neurodevelopmental disorders, metabolic diseases, and autoimmune disorders. The scope also includes the challenges and incentives related to orphan drug development, regulatory processes, and patient access to these treatments.
Based on the Think.Check.Submit framework by DOAJ, COPE & OASPA. All data from verified open sources.
Publication & Citation Trend
Articles published
Times cited
2017
2018
2019
2020
2021
2022
2023
2024
Source: OpenAlex · Note: citations accumulate over time so older years appear higher
SJR Quartile by Discipline
Scimago ranks this journal separately in each subject category — its quartile can differ by discipline.
Pharmacology, Toxicology and Pharmaceutics (miscellaneous)Q2
Health PolicyQ3
Pharmacology (medical)Q3
Subject Classification
Scopus Categories
Pharmacology (medical)Health PolicyPharmacology, Toxicology and Pharmaceutics (miscellaneous)
Research Topics (OpenAlex)
Lysosomal Storage Disorders ResearchGenomics and Rare DiseasesHealth Systems, Economic Evaluations, Quality of LifeLymphoma Diagnosis and TreatmentDiverse Scientific and Economic StudiesChronic Lymphocytic Leukemia ResearchNeurogenetic and Muscular Disorders ResearchHuman auditory perception and evaluationEducational Robotics and EngineeringPharmaceutical Economics and Policy